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Advancements and Obstacles of CRISPR-Cas9 Technology in Translational Research
Author: Liting You, Mengqian Li, Ruizhan Tong, Yuncong Liu, Jianxin Xue, You Lu
Journal: Molecular Therapy-Methods & Clinical Development, 2019, Vol., , DOI:10.1016/j.omtm.2019.02.008
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Rational Design of Gene Therapy Vectors
Author: Dao Pan, Hildegard Büning, Chen Ling
Journal: Molecular Therapy-Methods & Clinical Development, 2019, Vol.12, 246-247, DOI:10.1016/j.omtm.2019.01.009
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MicroRNA-96 Promotes Schistosomiasis Hepatic Fibrosis in Mice by Suppressing Smad7
Author: Xufeng Luo, Dongmei Zhang, Jun Xie, Qin Su, Xing He, Ruipu Bai, Guangping Gao, Weiqing Pan
Journal: Molecular Therapy-Methods & Clinical Development, 2018, Vol.11, 73-82, DOI:10.1016/j.omtm.2018.10.002
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P-FN12, an H4R-Based Epitope Vaccine Screened by Phage Display, Regulates the Th1/Th2 Balance in Rat Allergic Rhinitis
Author: Yuqian Wang, Jichao Sha, Heng Wang, Lifeng An, Tie Liu, Lin Li
Journal: Molecular Therapy-Methods & Clinical Development, 2018, Vol.11, 83-91, DOI:10.1016/j.omtm.2018.09.004
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A Robust System for Production of Superabundant VP1 Recombinant AAV Vectors
Author: Qizhao Wang, Zhongren Wu, Junping Zhang, Jenni Firrman, Hongying Wei, Zhengjing Zhuang, LinShu Liu, Linqing Miao, Yang Hu, Dong Li, Yong Diao, Weidong Xiao
Journal: Molecular Therapy-Methods & Clinical Development, 2017, Vol.7, 146-156, DOI:10.1016/j.omtm.2017.11.002
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Production and clinical development of nanoparticles for gene delivery
Author: Jie Chen, Zhaopei Guo, Huayu Tian, Xuesi Chen
Journal: Molecular Therapy-Methods & Clinical Development, 2016, Vol.3, 16023, DOI:10.1038/mtm.2016.23
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Syngeneic AAV Pseudo-particles Potentiate Gene Transduction of AAV Vectors
Author: Qizhao Wang, Biao Dong, Katie A. Pokiniewski, Jenni Firrman, Zhongren Wu, Mario P.S. Chin, Xiongwen Chen, LinShu Liu, Ruian Xu, Yong Diao, Weidong Xiao
Journal: Molecular Therapy-Methods & Clinical Development, 2017, Vol.4, 149-158, DOI:10.1016/j.omtm.2016.12.004
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Increasing the minicircle DNA purity using an enhanced triplex DNA technology to eliminate DNA contaminants
Author: Xiaohu H Hou, Xiaoyan Y Guo, Yusheng Chen, Cheng-Yi He, Zhi-Ying Chen
Journal: Molecular Therapy-Methods & Clinical Development, 2015, Vol.2, 14062, DOI:10.1038/mtm.2014.62